Working together to maximize the benefit to patients
Drug development is a team endeavor. We continuously explore strategic collaborations with like-minded partners to expand our pipeline of product candidates and to advance RNAi medicines toward commercialization for the treatment of both rare and common diseases.
We use RNA interference, or RNAi, to create medicines that silence the genes that cause or contribute to disease. Our goal is to provide life-changing therapies to people living with rare and common diseases.